Sarepta Therapeutics (NASDAQ:SRPT) has hired a lobbying firm with close ties to the Trump administration as regulatory ...

US Food and Drug Administration Commissioner Marty Makary said he’s trying to persuade Vinay Prasad, the agency’s former head ...

CGT Global, a leading biotechnology company driving the development and delivery of innovative cell and gene therapies, today ...

Currently, GenAns Biotech is conducting investigator-initiated trials for several gene therapies, including GA001 for ...

A 26-year-old Downriver man seen at Children’s Hospital of Michigan in Detroit since infancy for a rare bleeding disorder in ...

The Revell family hoped a gene therapy could buy time for their sons, who have a rare and fatal disease. After two patients ...

The primary safety risks associated with gene therapy include immune reactions and off-target effects in unintended organs, ...

Parents of boys with Duchenne muscular dystrophy weigh in on drug innovation and medical regulation.

Gene therapy has been headline news in recent years, in part due to the rapid development of biotechnology that enables doctors to administer such treatments. Broadly, gene therapies are ...

Leveraging Northway Biotech’s 20+ years of CDMO expertise, Diorasis Therapeutics is advancing AAV gene therapy for glaucoma ...

Gene therapy appears to be a promising approach for a subset of genetic deafness, although challenges remain with development ...

Gene therapy is a revolutionary field in modern medicine, offering transformative potential to treat and potentially cure a wide range of genetic and acquired diseases. By addressing the root ...