Neurology encompasses a vast spectrum of disorders that affect the central and peripheral nervous systems, with neuromuscular diseases representing a significant subgroup. These disorders include ...
-- Muscular Dystrophy Association Calls FDA Approval of Novartis' Itvisma (onasemnogene abeparvovec-brve) a Major Step Forward for the Spinal Muscular Atrophy Community Mary Fiance, National Vice ...
MDA’s partnership in research includes collaborative research grants with the ALS Network, Cure ADSSL1, Coalition to Cure ...
The FDA approved Itvisma gene therapy for patients aged 2 years and older with spinal muscular atrophy and confirmed SMN1 ...
Gene editing, AI, and platform technology offer significant opportunities in neuromuscular disease research despite systemic challenges. Robert Califf, MD, highlighted the need for multidisciplinary ...
A UConn professor and researcher who 28 years ago discovered a gene for a protein that limits human muscle growth is closer than ever to having that work play a significant role in treating those with ...
Using two smartphone cameras and a free video app, a detailed intervention can be produced with accuracy for diagnosing neuromuscular diseases. The innovative discovery was made by researchers from ...
The FDA approved an intrathecal form of Novartis’ spinal muscular atrophy gene therapy Zolgensma on Monday, broadening access ...
THURSDAY, Oct. 23, 2025 (HealthDay News) — Autoimmune neuromuscular diseases may sound complex, but understanding them is the first step to getting the right care and support. Conditions such as ...
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